A STUDY FOR PATIENTS WITH SPINAL MUSCULAR ATROPHY

Novartis Gene Therapies SMA (MAP-RESTORE-Country Specific Protocols) is a study for patients who have been diagnosed with spinal muscular atrophy (SMA). Approximately 500 patients with SMA from around the world will join the study.

The main purpose of the study is to evaluate the effectiveness of treatments for SMA over time. The study will also look at how SMA and treatment affect the health and quality of day-to-day life.

This website is for participating sites, patients, and their parents/legal guardians who are participating in Novartis Gene Therapies SMA (MAP-RESTORE-Country Specific Protocols).

If you are a patient or parent/legal guardian of a patient taking part in the study and have any questions, please contact your study doctor.